Twenty “must-read” publications from 2020
#1 to #3: Gene therapy and X reactivation: Gene replacement ameliorates deficits in mouse and human models of cyclin-dependent kinase-like 5 disorder. Gao Y et al., Brain Proof-of-concept for a gene replacement approach to CDKL5 deficiency disorder. Benke TA and Kind PC, Brain First published proof of concept for AAV-mediated gene therapy…